A Summerville man became the first person in South Carolina to undergo potentially life-changing gene therapy. The treatment took place Thursday morning at Prisma Health's Hemophilia Treatment Center ...
Oct. 14, 2024 – The FDA has approved a new preventive treatment for people with certain types of hemophilia that can reduce bleeding episodes, sometimes down to just a few per year.
Joint damage and chronic pain persist in hemophilia, especially in low-resource settings, necessitating innovative therapies and early diagnostic tools. Extended half-life products and emerging ...
As many as 30% of people living with severe hemophilia A develop inhibitors such as TFPI, which can be produced by the body’s immune response to clotting factors in replacement therapy, often limiting ...
The approval is based on an open-label, multicenter study of 116 adult and pediatric male patients with either severe hemophilia A or severe hemophilia B, both without inhibitors. For the first ...
FIX in hemophilia B), impacting more than 800,000 people globally. Results from the Phase 3 BASIS trial (NCT03938792) supported the FDA approval of Hympavzi. In the study, Hympavzi reduced the ...